In: Biology
Which one is a good candidate for gene therapy using recombinant DNA technology (introducing a new gene into the body to help fight a disease), the Huntington disease or cystic fibrosis? Why?
Cystic fibrosis is good candidate for gene therapy using recombinant DNA technology , because A new partnership in the UK will develop a gene therapy for cystic fibrosis that could treat the disease with a single dose. Cystic fibrosis is a genetic disease that causes mucus to build up in a patient's lungs. As a result, patients suffer from blocked airways and bacterial infections.
Huntington's disease is caused by the abnormal repetition of a specific DNA sequence at the tail end of the huntingtin gene. This defective mutant gene causes production of a toxic protein that progressively accumulates and damages the patient's neurons. There is currently no cure for Huntington's disease